The new findings strengthen the "RNA world" hypothesis that describes how the first life on Earth could have used RNA instead ...

Aperture Therapeutics is advancing APRTX-003, an RNA-based antisense therapy targeting MMP9, as a potential ALS treatment.

Veteran immunologist and former Pfizer R&D leader joins Circurna to advance its circular RNA therapeutic platform ...

Researchers from Radboud university medical center and University of Basel have discovered new genetic causes of inherited ...

Advancing RNA therapeutics depends on understanding two critical questions: Where do drug candidates go, and what do they do ...

The technology, called the Viral-Engineered RNA-based Activation System (VERAS), hijacks the virus's own replication ...

Retinitis pigmentosa (RP) is a genetic eye disorder affecting around one in 5,000 people worldwide. It typically begins with ...

Codexis Inc. and Axolabs have entered into an agreement under which Axolabs will evaluate Codexis’ ECO Synthesis ...

Aurora Therapeutics, cofounded by Nobel Prize–winning scientist Jennifer Doudna, plans to use gene editing and a new FDA ...

The companies didn’t provide details, but said global regulatory filings are now planned for the therapy, an oligonucleotide ...

Pancreatic ductal adenocarcinoma (PDAC) is the most lethal form of pancreas cancer. It's also the most common form of the ...

Scientists have discovered a new CRISPR mechanism with precise activity, expanding the potential applications of the existing ...